Downloadable information for your patients and families to learn more about the genetic disorders that cause homocystinuria and instructions on how to take CYSTADANE.
The following educational and advocacy groups provide information about rare genetic disorders, including the different types of homocystinuria. You can explore these groups online.
The mission of HCU Network America is to help people with homocystinuria (HCU) and related disorders manage their disease and to find a cure.
The Organic Acidemia Association is a patient advocacy organization that provides support and information for people with inherited metabolic disorders. Homocystinuria caused by several cobalamin defects—cblC, cblD, cblF, cblJ, and cblX—is included as a part of the group’s advocacy activities.
Cystadane is a methylating agent indicated in pediatric and adult patients for the treatment of homocystinuria to decrease elevated homocysteine blood concentrations. Included within the category of homocystinuria are: